UCD / OTC Clinical Trials

CanPKU+ is very active in helping in any we can in order to advancing the UCD/OTC Tool box by working with clinical trials in order to get more in the tool box.

We celebrate those who participate in these trials for the betterment of all those with PKU. Thank you!

Arcturus RX - For more information visit https://otcmrnastudy.com/en/. 

To download PDF click HERE

Bloomsbury Genetic Therapies clinical trail - gene therapy for OTC

Please note, this clinical trial is for ages 6 to 16. The second phase will be for newborns to 16 years old. The trial is based in London, UK, however it is open to Canadians and travel costs will potentially be covered.

For more information, visit the Metabolic Support UK website or email contact@metabolicsupportuk.org. 

We thank those who participate in clinical trials for UCDs for the betterment of the community.

CommuniKIDS team was thrilled to share the finalized trial results template and “tip sheet”  They hope that the template which was developed together will be used widely and will be helpful to youth and their families after participating in a clinical trial. This was officially launched on the CTO website this Friday, May 20^th, 2022 on International Clinical Trials Day, where trialists will be able to download the template for their own use to communicate trial results back to youth and their families. They expect it to be available in french by the summer of 2022. They acknowledge and thank those who provided input including 5 youth advisors, Allison, Chloe, Jessica, Rhys, and Samarah, and 8 parent advisors, including Katrina Hill, Karen Ladner Haas, Lynn Mendonza, Ryan LaPointe, Tanya Chute Nagy, and Yan Défossés. This work was supported by the CHILD-BRIGHT KT Innovation Knowledge Incubator grant.